List of our PhD projects
- DC1: Pipeline to identify cryptic splice variants and skippable exons at large scale
- DC2: Small scale ASO production
- DC3: Clinical, research and health care ethics for tailored genetic treatments
- DC4: Development and efficacy testing of a cryptic splice ASO (use case ATM)
- DC5: Development and efficacy testing of an exon skipping ASO (use case BPAN)
- DC6: ASO iPSc toxicity screen in vitro
- DC7: ASO safety studies in rat in an academic setting
- DC8: Individually tailored digital-motor outcomes in real life
- DC9: Individually tailored molecular treatment response profiling
- DC10: Statistical methodologies to evaluate efficacy of tailored single-patient treatments